BioMarin Pharmaceutical

Results: 48



#Item
21Pharmaceutical sciences / Pharmacology / Industrial engineering / Food and Drug Administration / BioMarin Pharmaceutical / Packaging and labeling / Validation / Carton / Form FDA 483 / Technology / Quality / Business

Review - Laronidase (Aldurazyme)

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Source URL: www.fda.gov

Language: English
22Pharmaceutical sciences / Biotechnology / Pharmaceutical industry / Biologic / Specification / Mucopolysaccharidosis / Test method / Recombinant DNA / BioMarin Pharmaceutical / Science / Pharmacology / Quality

Review - Laronidase (Aldurazyme)

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Source URL: www.fda.gov

Language: English
23Mucopolysaccharidosis / Hurler syndrome / Placebo / Hunter syndrome / Clevidipine / Medicine / Health / Syndromes

Laronidase (Aldurazyme), Biomarin Pharmaceutical Inc

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Source URL: www.fda.gov

Language: English
24Rare diseases / Drug discovery / Orphan drug / Pharmaceuticals policy / Morquio syndrome / Pharmaceutical industry / BioMarin Pharmaceutical / Mucopolysaccharidosis / National Organization for Rare Disorders / Health / Pharmaceutical sciences / Medicine

National Organization for Rare Disorders Remarks before the FDA Endocrinologic and Metabolic Drugs Advisory Committee Silver Spring, Maryland November 19, 2013 Good afternoon. My name is Diane Edquist Dorman, Vice Presid

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Source URL: rarediseases.org

Language: English - Date: 2013-11-22 12:36:21
25Environmental engineering / Water / Earth / Aquatic ecology / Environmental science / BioMarin Pharmaceutical / Wastewater / Clean Water Act / Effluent / Water pollution / Environment / Sewerage

BioMarin Clean Water Act Inspection Report, June 2007

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Source URL: www.epa.gov

Language: English - Date: 2012-04-09 11:15:57
26Peptide hormones / Hepatology / Glycogen storage disease type II / Mannose 6-phosphate / Insulin-like growth factor 1 / Insulin-like growth factor / BioMarin Pharmaceutical / Lysosomal storage disease / Alpha-glucosidase / Biology / Cell biology / Growth factors

Molecular Bases of Disease: Glycosylation-independent Lysosomal Targeting of Acid α-Glucosidase Enhances Muscle Glycogen Clearance in Pompe Mice John A. Maga, Jianghong Zhou, Ravi Kambampati, Susan Peng, Xu Wang, Richar

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Source URL: amdapompe.ehclients.com

Language: English - Date: 2013-07-21 20:12:27
27Genetic genealogy / BioMarin Pharmaceutical / Glycogen storage disease type II / Acid alpha-glucosidase / Lysosomal storage disease / Mucopolysaccharidosis / Alglucosidase alfa / Neuronal ceroid lipofuscinosis / Tetrahydrobiopterin / Health / Rare diseases / Medicine

Contact: Investors: Traci McCarty BioMarin Pharmaceutical Inc[removed]

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Source URL: amdapompe.ehclients.com

Language: English - Date: 2014-06-08 18:46:42
28Mental retardation / Phenylketonuria / Hyperphenylalanemia / Newborn screening / Medical genetics / Tetrahydrobiopterin / Phenylalanine / PKU / BioMarin Pharmaceutical / Medicine / Health / Pediatrics

Review © American College of Medical Genetics and Genomics Open

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Source URL: www.nature.com

Language: English - Date: 2013-08-27 17:07:39
29Economy of New York City / Financial data vendors / Business / Thomson Reuters / BioMarin Pharmaceutical / GTx Incorporated / Sunesis Pharmaceuticals / Pharmaceutical industry in India / Economy of the United States / NASDAQ / Medicine

  PRESS RELEASE For Immediate Release Contact Information: Thomas Carey

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Source URL: www.biocenturytv.com

Language: English - Date: 2012-09-21 12:16:24
30Temozolomide / PARP1 / Poly ADP ribose polymerase / Ewing sarcoma / BioMarin Pharmaceutical / Medicine / Oncology / PARP inhibitor

Microsoft PowerPoint - BMN 673 AACR-NCI-EORTC poster[removed]2013E-1

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Source URL: pptp.nchresearch.org

Language: English - Date: 2013-10-19 06:56:05
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